Samia P, Kirton A, Dale R, Tenembaum S, Triki CC, Hegde A, et al. Position Statement:Emerging genetic therapies for rare disorders: Genetic therapies. JICNA [Internet]. 2019 Jul. 25 [cited 2025 Mar. 29];1(1). Available from: https://jicna.org/index.php/journal/article/view/jicna-2019-172