Samia, Pauline, Adam Kirton, Russell Dale, Silvia Tenembaum, Chahnez Charfi Triki, Anaita Hegde, Richard Idro, Edward Kija, Jo M Wilmshurst, Ingrid Tein, and Haluk Topaloğlu. “Position Statement:Emerging Genetic Therapies for Rare Disorders: Genetic Therapies”. Journal of the International Child Neurology Association 1, no. 1 (July 25, 2019). Accessed April 18, 2024. https://jicna.org/index.php/journal/article/view/jicna-2019-172.