SAMIA, Pauline et al. Position Statement:Emerging genetic therapies for rare disorders: Genetic therapies. Journal of the International Child Neurology Association, [S. l.], v. 1, n. 1, 2019. DOI: 10.17724/jicna.2019.172. Disponível em: https://jicna.org/index.php/journal/article/view/jicna-2019-172. Acesso em: 29 mar. 2025.